Research programme: ribosomal protein modulators - Eloxx Pharmaceuticals
Alternative Names: ERSG molecules - Eloxx Pharmaceuticals; Eukaryotic ribosomal selective glycosides - Eloxx PharmaceuticalsLatest Information Update: 04 Aug 2023
At a glance
- Originator Technion - Israel Institute of Technology
- Developer Eloxx Pharmaceuticals
- Class Eye disorder therapies; Glycosides; Small molecules
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator stimulants; Ribosomal protein modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Cystic fibrosis
- Discontinued Autosomal dominant polycystic kidney disease; Cystinuria; Eye disorders; Inborn genetic disorders; Lung disorders
Most Recent Events
- 04 Aug 2023 Discontinued - Preclinical for Autosomal dominant polycystic kidney disease in Israel (unspecified route) (before August 2023) (Eloxx Pharmaceuticals Pipeline, August 2023)
- 04 Aug 2023 Discontinued - Preclinical for Cystinuria in Israel (unspecified route) (before August 2023) (Eloxx Pharmaceuticals Pipeline, August 2023)
- 04 Aug 2023 Discontinued - Preclinical for Eye disorders in Israel (Intravitreous) (before August 2023) (Eloxx Pharmaceuticals Pipeline, August 2023)