Research programme: Adeno associated virus vectored gene therapies - Sio Gene Therapies/Benitec Biopharma
Alternative Names: AXO-AAV-ALS; AXO-AAV-FTD; AXO-AAV-TBDLatest Information Update: 28 Aug 2022
At a glance
- Originator Benitec Biopharma
- Developer Benitec Biopharma; Sio Gene Therapies
- Class Gene therapies; Small interfering RNA
- Mechanism of Action Gene transference; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Amyotrophic lateral sclerosis; Dementia
Most Recent Events
- 28 Aug 2022 No recent reports of development identified for research development in Amyotrophic-lateral-sclerosis in Australia
- 28 Aug 2022 No recent reports of development identified for research development in Dementia in Australia
- 10 Nov 2020 Axovant Gene Therapies is now called Sio Gene Therapies