Drug Profile
RGX 121
Alternative Names: RGX-121Latest Information Update: 12 Feb 2024
Price :
$50
*
At a glance
- Originator REGENXBIO
- Class Gene therapies
- Mechanism of Action Gene transference; Iduronate sulfatase replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase II/III Mucopolysaccharidosis II