Sirolimus - Emtora Biosciences
Alternative Names: Encapsulated rapamycin; Encapsulated rapamycin - Emtora Biosciences; eRapa™Latest Information Update: 02 Jul 2025
At a glance
- Originator University of Texas Health Science Center at San Antonio
- Developer Emtora Biosciences
- Class Anti-infectives; Anti-inflammatories; Antiepileptic drugs; Antifungals; Antineoplastics; Cardiovascular therapies; Eye disorder therapies; Lactones; Macrolides; Nootropics; Polyenes; Pyridines; Skin disorder therapies
- Mechanism of Action Immunosuppressants; Methylmalonyl CoA mutase stimulants; MTOR protein inhibitors; T lymphocyte inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase III Familial adenomatous polyposis
- Phase II Bladder cancer
- Phase I Prostate cancer
- No development reported Autoimmune disorders; Breast cancer; Cognition disorders; Lung cancer
Most Recent Events
- 25 Jun 2025 Phase-III clinical trials in Familial adenomatous polyposis in USA (PO) (NCT06950385)
- 23 Jun 2025 Biodexa Pharmaceuticals plans a phase III Serenta trial for Familial adenomatous polyposis in USA and Europe in the first quarter of 2025 (PO) (NCT06950385)
- 12 May 2025 Sirolimus - Emtora Biosciences receives Orphan Drug status for Familial adenomatous polyposis in European Union