BI 3720931
Alternative Names: BI-3720931; Cystic fibrosis gene therapy - Boehringer Ingelheim/Oxford BioMedica/the UK Cystic Fibrosis Gene Therapy ConsortiumLatest Information Update: 12 Jun 2025
At a glance
- Originator The UK Cystic Fibrosis Gene Therapy Consortium
- Developer Boehringer Ingelheim
- Class Gene therapies
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Cystic fibrosis
Most Recent Events
- 20 May 2025 Boehringer Ingelheim initiates the phase I/II trial in Cystic fibrosis in United Kingdom (Inhalation) (NCT06962852)
- 13 May 2025 Boehringer Ingelheim plans the phase I/II Lenticlair™-ON trial in Cystic fibrosis in France, Italy, Netherlands, Spain, United Kingdom (Inhalation) (NCT06962852) (EUCT2023-504909-37-00)
- 04 Nov 2024 Phase-I/II clinical trials in Cystic fibrosis in Spain, Netherlands, Italy, France, United Kingdom (Inhalation)(EudraCT2023-503281-23-00) (NCT06515002)