Research programme: CNS targeted gene therapies - Lacerta Therapeutics
Latest Information Update: 28 Jun 2024
At a glance
- Originator Lacerta Therapeutics
- Developer Lacerta Therapeutics; Sarepta Therapeutics
- Class Cardiovascular therapies; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Cardiomyopathies; CNS disorders; Glycogen storage disease type II; Multiple sclerosis
Most Recent Events
- 28 Jun 2024 No recent reports of development identified for preclinical development in Cardiomyopathies in USA (Parenteral)
- 28 Jun 2024 No recent reports of development identified for research development in Multiple-sclerosis in USA (Parenteral)
- 28 Sep 2022 No recent reports of development identified for research development in CNS-disorders in USA (Parenteral)