Deoxycytidine/deoxythymidine - Modis Therapeutics
Alternative Names: dC/dT - Modis Therapeutics; Deoxycytidine/deoxythymidine; Doxecitine/Doxribtimine - UCB; doxTM; MT 1621 - UCB; MT-1621; Thymidine/deoxycytidine - Modis TherapeuticsLatest Information Update: 31 Mar 2025
At a glance
- Originator Columbia University Medical Center; Vall d-Hebron Research Institute
- Developer Columbia University Medical Center; Modis Therapeutics; Vall d-Hebron Research Institute
- Class Deoxyribonucleosides; Small molecules
- Mechanism of Action Deoxyribonucleoside replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preregistration Mitochondrial disorders
Most Recent Events
- 31 Mar 2025 Preregistration for Mitochondrial disorders (In adolescents, In children, In the elderly, In adults) in USA (PO)
- 31 Mar 2025 Preregistration for Mitochondrial disorders in European Union (PO)
- 31 Mar 2025 Deoxycytidine/deoxythymidine receives priority review status for Mitochondrial disorders in USA