Human hydroxymethylbilane synthase encoding mRNA - Moderna Therapeutics
Alternative Names: hPBGD mRNA - Moderna TherapeuticsLatest Information Update: 28 Jul 2022
At a glance
- Originator Moderna Therapeutics
- Developer Center for Applied Medical Research; Moderna Therapeutics
- Class RNA
- Mechanism of Action Hydroxymethylbilane synthase stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Acute intermittent porphyria
Most Recent Events
- 28 Jul 2022 No recent reports of development identified for preclinical development in Acute-intermittent-porphyria in Spain (IV)
- 08 Oct 2018 Preclinical data for Acute intermittent porphyria released by Moderna Therapeutics
- 01 Jun 2018 Preclinical trials in Acute intermittent porphyria in Spain (IV)