Research programme: stereopure oligonucleotide therapeutics - Wave Life Sciences
Alternative Names: Stereopure oligonucleotide therapeuticsLatest Information Update: 28 Nov 2022
At a glance
- Originator WaVe life Sciences
- Class Antisense oligonucleotides; Eye disorder therapies; Nucleic acids
- Mechanism of Action ABCA4 protein modulators; Cep290 protein modulators; Gene expression modulators; Rho-associated kinase modulators; RNA interference; USH2A protein modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Leber congenital amaurosis; Retinitis pigmentosa; Stargardt disease; Usher syndromes
Most Recent Events
- 28 Nov 2022 No recent reports of development identified for research development in Leber-congenital-amaurosis in USA (Intravitreous, Injection)
- 28 Nov 2022 No recent reports of development identified for research development in Retinitis-pigmentosa in USA (Intravitreous, Injection)
- 28 Nov 2022 No recent reports of development identified for research development in Stargardt disease in USA (Intravitreous, Injection)