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ABO 401

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Drug Profile

ABO 401

Alternative Names: ABO-401; AIM™ AAV204 CFTR; AIM™ AAV204.CFTR

Latest Information Update: 28 Jul 2022

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At a glance

  • Originator Abeona Therapeutics
  • Class Gene therapies
  • Mechanism of Action Cystic fibrosis transmembrane conductance regulator stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • No development reported Cystic fibrosis

Most Recent Events

  • 28 Jul 2022 No recent reports of development identified for preclinical development in Cystic-fibrosis in USA (Parenteral)
  • 20 Jan 2020 University of North Carolina’s (UNC) has patent protection for adeno-associated virus (AAV) vectors targeted for central nervous system
  • 20 Jan 2020 University of North Carolina’s (UNC) has patents pending for Abeona's AAV204 based gene therapy vector compositions .

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