Research programme: gene editing therapeutics - Arbor Biotechnologies/Vertex Pharmaceuticals
Latest Information Update: 28 Feb 2023
At a glance
- Originator Arbor Biotechnologies
- Class Antifibrotics; Gene therapies; Proteins
- Mechanism of Action Gene modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research CNS disorders
- No development reported Cystic fibrosis
Most Recent Events
- 28 Feb 2023 No recent reports of development identified for research development in Cystic-fibrosis in USA
- 09 Nov 2021 Early research in CNS disorders in USA (unspecified route)
- 03 Jan 2019 Arbor Biotechnologies and Vertex Pharmaceuticals entered into a research collaboration to develop gene editing therapeutics for Cystic fibrosis