Research programme: antisense oligonucleotide therapies - NeuBase Therapeutics
Alternative Names: DM1 investigational genetic therapy; NT0100; NT0200Latest Information Update: 28 Sep 2023
At a glance
- Originator NeuBase Therapeutics
- Class Antisense DNA; Antisense oligonucleotides; Antisense RNA
- Mechanism of Action RNA interference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Myotonic dystrophy
- No development reported Huntington's disease; Neurological disorders
Most Recent Events
- 28 Sep 2023 No recent reports of development identified for preclinical development in Huntington's-disease in USA (SC)
- 28 Sep 2023 No recent reports of development identified for preclinical development in Myotonic dystrophy in USA (SC)
- 28 Feb 2023 No recent reports of development identified for research development in Neurological-disorders in USA (Parenteral)