AVXS 501
Alternative Names: AVXS-501Latest Information Update: 28 Feb 2023
Price :
$50 *
At a glance
- Originator AveXis
- Developer Novartis Gene Therapies
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Unspecified