PPY 988
Alternative Names: GT-005; PPY-988Latest Information Update: 22 Sep 2023
At a glance
- Originator Gyroscope Therapeutics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Complement factor I replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Dry macular degeneration
Most Recent Events
- 14 Sep 2023 Gyroscope Therapeutics terminates phase I/II FOCUS trial in Dry macular degeneration in the US and United Kingdome (Intraocular) (NCT03846193)
- 14 Sep 2023 Discontinued - Phase-II for Dry macular degeneration in Australia (Intraocular)
- 14 Sep 2023 Discontinued - Phase-II for Dry macular degeneration in Spain (Intraocular)