QRX 136
Alternative Names: QRX-136Latest Information Update: 16 Mar 2023
At a glance
- Originator ProQR Therapeutics
- Class Eye disorder therapies; Oligonucleotides; Small interfering RNA
- Mechanism of Action RNA interference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Leber congenital amaurosis
Most Recent Events
- 14 Mar 2023 The European Patent Office (EPO) dismisses oppositions filed against ProQR Therapeutics for patent related to Axiomer® technology in the European Union
- 28 Feb 2023 No recent reports of development identified for research development in Leber-congenital-amaurosis in Netherlands
- 31 Dec 2022 ProQR Therapeutics has patent pending for Axiomer® platform in Australia, Brazil, India, and the US (divisional application)