Avigbagene parvec - Spur Therapeutics
Alternative Names: FLT-200; FLT-201; FLT200/201Latest Information Update: 11 May 2026
At a glance
- Originator University College London
- Developer Spur Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference; Glucosylceramidase replacements
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Orphan Drug Status
Yes - Gaucher's disease type I
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase III Gaucher's disease type I
Most Recent Events
- 04 May 2026 Pooled efficacy data from a phase I/II GALILEO-1 and GALILEO-2 trial in Gaucher's disease type I released by Spur Therapeutics
- 04 Feb 2026 Phase-III clinical trials in Gaucher's disease type I (Treatment-experienced) in United Kingdom, Israel, Canada, Argentina (IV) (NCT07223944)
- 04 Feb 2026 Phase-III clinical trials in Gaucher's disease type I (Treatment-experienced) in the US (IV) (NCT07223944)