FLT 201
Alternative Names: FLT-200; FLT-201; FLT200/201Latest Information Update: 29 Oct 2024
At a glance
- Originator University College London
- Developer Spur Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference; Glucosylceramidase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Gaucher's disease type I
Most Recent Events
- 23 Oct 2024 Efficacy, adverse events and pharmacodynamics data from the phase I/II GALILEO-1 trial in Gaucher’s disease type I released by Spur Therapeutics
- 08 Jul 2024 Efficacy and adverse events data from phase-I/II GALILEO-1 trial released by Spur Therapeutics
- 08 Jul 2024 Spur Therapeutics completes enrolment in the phase-I/II GALILEO-1 trial for Gaucher's disease in USA, Brazil, Germany, Israel, Spain, Paraguay and United Kingdom (IV) (NCT05324943)