Fidrisertib - Ipsen
Alternative Names: BLU-782; IPN-60130Latest Information Update: 05 Nov 2023
Price :
$50 *
At a glance
- Originator Blueprint Medicines
- Developer Blueprint Medicines; Ipsen
- Class Carbamates; Furans; Piperazines; Piperidines; Pyridazines; Pyridines; Pyrroles; Small molecules
- Mechanism of Action ACVR1 protein inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase II Fibrodysplasia ossificans progressiva
Most Recent Events
- 01 Dec 2021 Phase-II clinical trials in Fibrodysplasia ossificans progressiva (In adolescents, In children, In the elderly, In adults) in Germany, Netherlands, Spain, United Kingdom, USA (PO) after December 2021 (NCT05039515) (EudraCT2020-002858-24)
- 01 Dec 2021 Phase-II clinical trials in Fibrodysplasia ossificans progressiva (In adults, In the elderly, In adolescents, In children) in Italy, Sweden (PO) (EudraCT2020-002858-24) (NCT05039515)
- 17 Feb 2021 Phase-II clinical trials in Fibrodysplasia ossificans progressive in USA (PO), prior to February 2021 (Ipsen pipeline, February 2021)