DYST 201
Alternative Names: DYST-201; Huntington’s disease gene therapy - Dystrogen TherapeuticsLatest Information Update: 03 Dec 2019
At a glance
- Originator Dystrogen Therapeutics
- Class Gene therapies; Small interfering RNA
- Mechanism of Action Gene transference; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Huntington's disease