Research programme: glucocerebrosidase targeting therapies - Gain Therapeutics
Alternative Names: GBA programme - Gain Therapeutics; GBA-related diseases therapeutics - Gain TherapeuticsLatest Information Update: 28 Mar 2024
At a glance
- Originator Gain Therapeutics
- Class Antiparkinsonians; Pharmacological chaperones; Small molecules
- Mechanism of Action Glucosylceramidase stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Gaucher's disease; Parkinson's disease
Most Recent Events
- 28 Mar 2024 No recent reports of development identified for preclinical development in Gaucher's-disease in USA (PO)
- 28 Mar 2024 No recent reports of development identified for preclinical development in Parkinson's-disease in USA (PO)
- 12 Apr 2023 Gain Therapeutics plans a clinical trials for Parkinson's disease in 2023