GNR 055
Alternative Names: GNR-055Latest Information Update: 04 Jul 2024
At a glance
- Originator GENERIUM Pharmaceuticals
- Class Iduronate sulfatases; Recombinant proteins
- Mechanism of Action Iduronate sulfatase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase II/III Mucopolysaccharidosis II
Most Recent Events
- 20 Sep 2023 GENERIUM Pharmaceuticals completes a phase I trial in Mucopolysaccharidosis II (In volunteers) in Russia (IV, Injection) (NCT06475404)
- 06 Apr 2023 GENERIUM Pharmaceuticals initiates a phase I trial in Mucopolysaccharidosis II (In volunteers) in Russia (IV, Injection) (NCT06475404)
- 30 Nov 2021 Phase-II/III clinical trials in Mucopolysaccharidosis II in Russia (IV) (NCT05208281)