Research programme: RNA splicing modifiers - Skyhawk Therapeutics/Takeda
Latest Information Update: 28 Jun 2023
At a glance
- Originator Skyhawk Therapeutics
- Class Small molecules
- Mechanism of Action RNA splicing modulators
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Neurological disorders
Most Recent Events
- 28 Jun 2023 No recent reports of development identified for research development in Neurological-disorders in USA
- 06 May 2019 RNA splicing modifiers licensed to Takeda worldwide for the treatment of Neurological disorders
- 06 May 2019 Early research in Neurological disorders in USA (unspecified route)