ASC 618
Alternative Names: Adeno-associated viral vector haemophilia A gene therapy - ASC Therapeutics; ASC-618; CRISPR/cas9 edited human factor VIII - ASC TherapeuticsLatest Information Update: 02 Sep 2022
At a glance
- Originator ASC Therapeutics
- Class Antihaemorrhagics; Blood coagulation factors; Gene therapies
- Mechanism of Action Factor VIII replacements; Gene transference
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Orphan Drug Status
Yes - Haemophilia A
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Haemophilia A