Research programme: neuromuscular gene therapies - Locanabio
Latest Information Update: 28 Oct 2024
At a glance
- Originator Locanabio
- Class Gene therapies
- Mechanism of Action RNA modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes
Highest Development Phases
- No development reported Inborn genetic disorders; Myotonic dystrophy
Most Recent Events
- 28 Oct 2024 No recent reports of development identified for preclinical development in Myotonic dystrophy in USA (IM, Injection)
- 28 Oct 2024 No recent reports of development identified for preclinical development in Myotonic dystrophy in USA (Parenteral, Injection)
- 28 Jun 2023 No recent reports of development identified for research development in Inborn genetic disorders in USA (Parenteral, Injection)