Research programme: congenital muscular dystrophy gene therapy - SEAL Therapeutics/Santhera Pharmaceuticals
Latest Information Update: 28 Jun 2023
At a glance
- Originator Biozentrum, University of Basel; Rutgers
- Developer Santhera Pharmaceuticals; SEAL Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference; Laminin alpha 2 replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Muscular dystrophies
Most Recent Events
- 28 Jun 2023 No recent reports of development identified for preclinical development in Muscular-dystrophies in Switzerland (Parenteral)
- 28 Feb 2022 Santhera Pharmaceuticals terminates a licensing agreement with Biozentrum,University of Basel for development of gene therapy for Muscular dystrophies
- 28 Feb 2022 Santhera Pharmaceuticals terminates a licensing agreement with Rutgers for development of gene therapy for Muscular dystrophies