AT 753
Alternative Names: AT-753Latest Information Update: 02 Aug 2022
At a glance
- Originator Audentes Therapeutics
- Developer Astellas Gene Therapies
- Class Antisense oligonucleotides; Gene therapies
- Mechanism of Action Dystrophin expression stimulants; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Duchenne muscular dystrophy
Most Recent Events
- 01 Aug 2022 Discontinued - Preclinical for Duchenne muscular dystrophy in USA (Parenteral) prior to August 2022
- 01 Apr 2021 Audentes Therapeutics is now called Astellas Gene Therapies
- 10 Dec 2020 Audentes Therapeutics plans to initiate clinical trials for Duchenne muscular dystrophy, in the 2021 financial year