AT 702
Alternative Names: AT-702; scAAV9 U7 ACCA - Astellas Gene Therapies; scAAV9.U7.ACCA - Astellas Gene TherapiesLatest Information Update: 02 Aug 2022
At a glance
- Originator Audentes Therapeutics
- Developer Astellas Gene Therapies
- Class Antisense oligonucleotides
- Mechanism of Action Dystrophin expression stimulants; RNA interference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Duchenne muscular dystrophy
Most Recent Events
- 01 Aug 2022 Discontinued - Phase-I/II for Duchenne muscular dystrophy (In children) in USA (IV) prior to August 2022 (NCT04240314)
- 01 Apr 2021 Audentes Therapeutics is now called Astellas Gene Therapies
- 15 Jan 2020 Phase-I/II clinical trials in Duchenne muscular dystrophy (In children) in USA (IV) (NCT04240314)