Research programme: AAV mediated antibody delivery gene therapies - REGENXBIO
Alternative Names: Gene therapies for hereditary angioedema - REGENXBIO; Hereditary angioedema gene therapy programme - REGENXBIOLatest Information Update: 16 Jun 2022
At a glance
- Originator REGENXBIO
- Class Gene therapies; Skin disorder therapies; Vascular disorder therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Hereditary angioedema