Research programme: apolipoprotein L1 inhibitors - Vertex Pharmaceuticals
Alternative Names: APOL1 inhibitors - Vertex PharmaceuticalsLatest Information Update: 28 Apr 2025
At a glance
- Originator Vertex Pharmaceuticals
- Class Small molecules; Urologics
- Mechanism of Action Apolipoprotein L1 inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Kidney disorders
Most Recent Events
- 28 Apr 2025 No recent reports of development identified for preclinical development in Kidney-disorders in USA (PO)
- 31 Jul 2019 Preclinical trials in Kidney disorders in USA (PO) before July 2019