Recombinant complement factor H - Disc Medicine
Alternative Names: GEM-103; rCFH; recombinant human CFH - Disc Medicine; rhCFH - Disc MedicineLatest Information Update: 02 Jan 2023
At a glance
- Originator Gemini Therapeutics
- Developer Disc Medicine
- Class Eye disorder therapies; Recombinant proteins
- Mechanism of Action Complement factor H replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase II Dry age-related macular degeneration; Wet age-related macular degeneration
Most Recent Events
- 29 Dec 2022 Gemini Therapeutics has merged with Disc Medicine to form Disc Medicine
- 01 Mar 2022 Gemini Therapeutics has pending patent cooperation treaty (PCT) application directed to dosage regimens for treating inflammatory ocular diseases using GEM 103 in the US and Undisclosed foreign locations
- 01 Mar 2022 Gemini Therapeutics has pending patent cooperation treaty (PCT) application directed to methods of treating age-related macular degeneration using GEM 103 in patients who carry certain CFH genetic mutations, in the US and Undisclosed foreign locations