Ribitol - ML Bio Solutions
Alternative Names: Adonitol; BBP 418Latest Information Update: 07 Aug 2024
At a glance
- Originator Atrium Health
- Developer ML Bio Solutions
- Class Small molecules; Sugar alcohols
- Mechanism of Action Glycosylation stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase III Limb girdle muscular dystrophies
Most Recent Events
- 01 Aug 2024 BridgeBio completes Type C meeting with the US FDA for Limb-girdle muscular dystrophies
- 18 Jun 2024 The US FDA has grants Rare Pediatric Disease Designation (RPDD) for BBP 418 in the treatment of Limb-girdle Muscular Dystrophy Type 2I/R9
- 31 Dec 2023 BridgeBio Pharma has multiple patents pending for methods of treatment, dosing methods, and compositions relating to ribitol in USA, Australia, Canada, Europe, China, Japan, and Mexico (SEC file 2023 - BridgeBio Pharma)