Research programme: NLRP3 antisense oligonucleotides - Ionis Pharmaceuticals
Alternative Names: NLRP3 ASOs - Ionis PharmaceuticalsLatest Information Update: 28 Jun 2023
At a glance
- Originator Ionis Pharmaceuticals
- Class Antifibrotics; Antisense oligonucleotides
- Mechanism of Action NLRP3 protein inhibitors; Protein synthesis inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Acute kidney injury; Idiopathic pulmonary fibrosis
Most Recent Events
- 28 Jun 2023 No recent reports of development identified for preclinical development in Idiopathic-pulmonary-fibrosis in USA (Endotracheal)
- 28 Jun 2023 No recent reports of development identified for preclinical development in Idiopathic-pulmonary-fibrosis(Prevention) in USA (Endotracheal)
- 28 Dec 2021 No recent reports of development identified for preclinical development in Acute kidney injury(Prevention) in USA (Parenteral)