mRNA 3927
Alternative Names: mRNA-3927Latest Information Update: 24 Jan 2024
At a glance
- Originator Moderna Therapeutics
- Class RNA
- Mechanism of Action Methylmalonyl-CoA decarboxylase expression stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Phase II Propionic acidaemia
Most Recent Events
- 08 Jan 2024 Moderna Therapeutics plans a pivotal trial for Propionic acidemia in 2024
- 09 Aug 2023 Phase-II clinical trials in Propionic acidaemia (In adolescents, In children, In the elderly, In infants, In adults) in Canada (IV) (Moderna Therapeutics pipeline, July 2023)
- 09 Aug 2023 Phase-II clinical trials in Propionic acidaemia (In adolescents, In children, In the elderly, In infants, In adults) in United Kingdom (IV) (Moderna Therapeutics pipeline, July 2023)