Research programme: genome editing therapies - Asklepios BioPharmaceutical/Editas Medicine
Latest Information Update: 28 Nov 2023
At a glance
- Originator Asklepios BioPharmaceutical; Editas Medicine
- Class
- Mechanism of Action Gene modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Neurological disorders
Most Recent Events
- 28 Nov 2023 No recent reports of development identified for research development in Neurological-disorders in USA (Parenteral)
- 15 Oct 2019 Asklepios BioPharmaceutical and Editas Medicine entered into a strategic research collaboration for development of genome editing therapies for neurological disorders
- 15 Oct 2019 Early research in Neurological disorders in USA (Parenteral)