Brogidirsen - Nippon Shinyaku
Alternative Names: Exon 44 skipping antisense oligonucleotide; Exon 44 skipping DMD therapeutic; NS-089/NCNP-02Latest Information Update: 17 Oct 2025
At a glance
- Originator Nippon Shinyaku
- Class Antisense oligonucleotides
- Mechanism of Action Dystrophin expression stimulants
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Orphan Drug Status
Yes - Duchenne muscular dystrophy
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Phase II Duchenne muscular dystrophy
Most Recent Events
- 14 Oct 2025 Efficacy and adverse events data from a phase II trial in Duchenne muscular dystrophy presented at the 30th annual International Congress of the World Muscle Society (WMS-2025)
- 05 Jan 2024 Phase-II clinical trials in Duchenne muscular dystrophy (In children, In adolescents) in USA (IV) (NCT05996003)
- 13 Dec 2023 Brogidirsen - Nippon Shinyaku receives Orphan Drug status for Duchenne muscular dystrophy in European Union