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Stargardt disease gene therapy - Spark Therapeutics

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Drug Profile

Stargardt disease gene therapy - Spark Therapeutics

Latest Information Update: 28 Nov 2023

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At a glance

  • Originator Spark Therapeutics
  • Class Eye disorder therapies; Gene therapies
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • No development reported Stargardt disease

Most Recent Events

  • 28 Nov 2023 No recent reports of development identified for research development in Stargardt disease in USA (Parenteral)
  • 17 Dec 2019 Spark Therapeutics has been acquired by Roche
  • 30 Oct 2019 Early research in Stargardt disease in USA (Parenteral) (Spark Therapeutics pipeline, October 2019)

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