DISC a
Alternative Names: DISC-a; DISC-BLatest Information Update: 28 Nov 2023
At a glance
- Originator Disc Medicine
- Class Antianaemics; Small molecules
- Mechanism of Action Matriptase inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Beta-thalassaemia; Haemochromatosis; Myelodysplastic syndromes
Most Recent Events
- 28 Nov 2023 No recent reports of development identified for preclinical development in Beta-thalassaemia in USA (PO)
- 28 Nov 2023 No recent reports of development identified for preclinical development in Haemochromatosis in USA (PO)
- 28 Nov 2023 No recent reports of development identified for preclinical development in Myelodysplastic-syndromes in USA (PO)