HMI 103
Alternative Names: HMI-103Latest Information Update: 27 Mar 2024
At a glance
- Originator Beckman Research Institute
- Developer Q32 Bio
- Class Gene therapies
- Mechanism of Action Gene transference; Phenylalanine ammonia lyase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes
Highest Development Phases
- Discontinued Phenylketonuria
Most Recent Events
- 25 Mar 2024 Q32 Bio has merged with Homology Medicines to form Q32 Bio
- 14 Sep 2023 Homology Medicines terminates a phase I pheEDIT trial for Phenylketonuria in USA (IV) as the Company discontinued the development of this program (NCT05222178)
- 27 Jul 2023 HMI 103 is available for licensing as of 27 Jul 2023. https://www.homologymedicines.com/pipeline/