Research programme: AAV-based gene therapies - Asklepios BioPharmaceutical/Cartesian Therapeutics
Latest Information Update: 28 Sep 2024
At a glance
- Originator Selecta Biosciences
- Developer Cartesian Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Glycogen storage disease type II; IgA nephropathy; Methylmalonic acidaemia; Primary biliary cirrhosis
Most Recent Events
- 28 Sep 2024 No recent reports of development identified for preclinical development in IgA-nephropathy in USA (Parenteral)
- 28 Sep 2024 No recent reports of development identified for preclinical development in Methylmalonic-acidaemia in USA (Parenteral)
- 28 Sep 2024 No recent reports of development identified for preclinical development in Primary-biliary-cirrhosis in USA (Parenteral)