STRX 230
Alternative Names: AAV-based Rett syndrome therapy - Sarepta Therapeutics/StrideBio; STRX-230Latest Information Update: 28 Dec 2023
At a glance
- Originator StrideBio
- Class Gene therapies
- Mechanism of Action Gene transference; Methyl-CpG-binding protein 2 expression stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Rett syndrome