STRX 210
Alternative Names: AAV-based NPC1 therapy- Sarepta Therapeutics/StrideBio; STRX-210Latest Information Update: 28 Sep 2025
At a glance
- Originator StrideBio
- Class Gene therapies
- Mechanism of Action Gene transference
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Niemann-Pick disease type C
Most Recent Events
- 28 Sep 2025 No recent reports of development identified for preclinical development in Niemann-Pick-disease-type-C in USA (Parenteral)
- 27 Aug 2021 Preclinical trials in Niemann-Pick disease type C in USA (Parenteral) (StrideBio pipeline, August 2021)
- 14 Nov 2019 StrideBio and Sarepta Therapeutics agree to co-develop Niemann-Pick disease gene therapies