STRX 210
Alternative Names: AAV-based NPC1 therapy- Sarepta Therapeutics/StrideBio; STRX-210Latest Information Update: 06 Sep 2021
At a glance
- Originator StrideBio
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Niemann-Pick disease type C