BMN 293
Alternative Names: BMN-293; DiNA-001; DINA-001/A; DINA-001/BLatest Information Update: 23 Apr 2024
At a glance
- Originator DiNAQOR AG
- Developer BioMarin Pharmaceutical; DiNAQOR AG
- Class Cardiovascular therapies; Gene therapies
- Mechanism of Action Gene transference; Myosin-binding protein C replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Hypertrophic cardiomyopathy
Most Recent Events
- 23 Apr 2024 Preclinical development is ongoing Switzerland (BioMarin Pharmaceutical pipeline, April 2024)
- 23 Apr 2024 Phase-I clinical trials in Hypertrophic cardiomyopathy (Intracardiac) before April 2024 (BioMarin Pharmaceutical pipeline, April 2024)
- 28 Feb 2024 No recent reports of development identified for preclinical development in Hypertrophic-cardiomyopathy in Switzerland (Intracardiac)