P OTC 101
Alternative Names: P-OTC-101Latest Information Update: 23 Apr 2025
At a glance
- Originator Poseida Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference; Ornithine carbamoyltransferase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes
Highest Development Phases
- Preclinical Ornithine carbamoyltransferase deficiency disease
Most Recent Events
- 10 May 2024 P OTC 101 is still in preclinical studies for Ornithine carbomoyltransferase deficiency disease in USA (parenteral)
- 31 Jul 2023 P OTC 101 receives Orphan Drug status for Ornithine carbamoyltransferase deficiency disease in USA
- 18 May 2023 Pharmacodynamics data from preclinical studies in Ornithine carbamoyltransferase deficiency disease released by Poseida Therapeutics