Research programme: repeat expansion disorders therapeutics - Triplet Therapeutics
Latest Information Update: 28 Aug 2024
At a glance
- Originator Triplet Therapeutics
- Class Antisense oligonucleotides; Small interfering RNA
- Mechanism of Action DNA damage modulators; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- No development reported Huntington's disease; Myotonic dystrophy; Spinocerebellar degeneration
Most Recent Events
- 28 Aug 2024 No recent reports of development identified for preclinical development in Huntington's-disease in USA (Parenteral)
- 28 Jan 2024 No recent reports of development identified for research development in Myotonic dystrophy in USA (Parenteral)
- 28 Jan 2024 No recent reports of development identified for research development in Spinocerebellar-degeneration in USA (Parenteral)