AVB 202
Alternative Names: AVB-202; AVB-202-TT; FXN gene therapy - Solid Biosciences; Gene therapy for Friedreich's Ataxia - Solid BiosciencesLatest Information Update: 28 Feb 2024
At a glance
- Originator AavantiBio
- Developer Solid Biosciences
- Class Gene therapies
- Mechanism of Action Frataxin protein replacements; Gene transference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Friedreich's ataxia
Most Recent Events
- 28 Feb 2024 No recent reports of development identified for preclinical development in Friedreich's ataxia in USA (Intrathecal, Injection)
- 28 Feb 2024 No recent reports of development identified for preclinical development in Friedreich's ataxia in USA (IV, Injection)
- 10 Jan 2023 Pharmacodynamics data from a preclinical study in Friedreich's ataxia released by Solid Biosciences