Research programme: RNA therapeutics - DTx Pharma
Alternative Names: MSUT2 programmeLatest Information Update: 28 Jun 2024
At a glance
- Originator DTx Pharma
- Class Antidementias; Antineoplastics; Antisense oligonucleotides; Cardiovascular therapies; Eye disorder therapies; RNA; Small interfering RNA
- Mechanism of Action RNA interference; Tau protein inhibitors
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Peripheral nervous system diseases
- Research Cancer; Cardiovascular disorders; Immunological disorders
- No development reported Alzheimer's disease; CNS disorders; Dementia; Eye disorders; Musculoskeletal disorders; Progressive supranuclear palsy; Retinitis pigmentosa
- Discontinued Duchenne muscular dystrophy
Most Recent Events
- 28 Jun 2024 No recent reports of development identified for preclinical development in Alzheimer's-disease in USA (Parenteral)
- 28 Jun 2024 No recent reports of development identified for preclinical development in Dementia in USA (Parenteral)
- 28 Jun 2024 No recent reports of development identified for preclinical development in Progressive-supranuclear-palsy in USA (Parenteral)