Guanidinoacetate methyltransferase erythrocyte encapsulated - Quince Therapeutics
Alternative Names: Ery-GAMT; Erythrocyte encapsulated GAMT; Erythrocyte encapsulated guanidinoacetate methyltransferase - Quince Therapeutics; GAMT erythrocyte encapsulated - Quince TherapeuticsLatest Information Update: 28 Mar 2024
At a glance
- Originator EryDel
- Developer Quince Therapeutics
- Class Enzymes
- Mechanism of Action Enzyme replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported CNS disorders