Research programme: SNA-based genetic disorder therapeutics - Exicure/Rosalind Franklin University of Medicine and Science
Latest Information Update: 10 Apr 2023
At a glance
- Originator Exicure; Rosalind Franklin University of Medicine and Science
- Developer Exicure
- Class Antisense elements; Immunotherapies; Nucleic acids; Oligonucleotides
- Mechanism of Action Gene expression modulators; Gene silencing; Immunomodulators
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Suspended Inborn genetic disorders
Most Recent Events
- 18 Feb 2020 Exicure has 135 pending patent applications and over 60 allowed or issued patents (Exicure website, February 2020)
- 13 Feb 2020 Exicure and Rosalind Franklin University of Medicine agree to co-develop SNA-based genetic disorder therapeutics for Inborn genetic disorders
- 13 Feb 2020 Early research in Inborn genetic disorders in USA (Parenteral)