Research programme: AAV-based gene therapeutics - Asklepios BioPharmaceutical/Cytoo
Latest Information Update: 28 Apr 2024
Price :
$50 *
At a glance
- Originator Asklepios BioPharmaceutical; CYTOO
- Developer Asklepios BioPharmaceutical
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Musculoskeletal disorders
Most Recent Events
- 28 Apr 2024 No recent reports of development identified for research development in Musculoskeletal-disorders in Scotland
- 28 Apr 2024 No recent reports of development identified for research development in Musculoskeletal-disorders in USA
- 04 Mar 2020 Asklepios BioPharmaceutical and Cytoo enteres into research agreement to select gene therapy candidates for rare muscle disorders